Gene Therapy Harvard Medical School Online

Overview

This advanced course in  Gene Therapy at Harvard Medical School Online offers a unique way for professionals to learn from leading Harvard Medical School faculty about gene therapy and about the advances happening in this field that are ultimately helping to improve the treatment of certain genetic diseases.

Background

In recent years, close collaboration between multiple scientific disciplines has rendered gene therapy a viable treatment option for some genetic conditions, and a promising pursuit for many others. As of today, there are numerous clinical trials underway for gene therapy treatments of various cancers, blood disorders, neurological diseases, and inherited retinal disorders to name a few. 

Advancements in vector science, gene editing technologies, and our understanding of the molecular underpinnings of disease continue to pave the way for the development of additional gene therapy treatments aimed at improving patient quality of life and prolonging lifespan. As this field continues to expand, so too will the number of genetic conditions that can be treated and possibly even cured with gene therapy making this an exciting time to delve into this field.